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U.S. Gene Therapy Trial for Thalassemia Receives FDA Approval

July17, 2012 Memorial Sloan-Kettering Cancer Center will begin evaluating a new stem-cell-based gene therapy for patients with the inherited blood disorder beta (β)-thalassemia. The clinical trial is the first to receive US Food and Drug Administration approval to treat this disease with genetically engineered cells and is a culmination of more than two decades of […]

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Results of Exjade for Non-Transfused Patients Study

December 16, 2011 – Results from THALASSA, a placebo-controlled study examining the benefit of iron chelation with Exjade® (deferasirox) in patients with non-transfusion-dependent thalassemia (NTDT), were presented on December 13 at the 53rd Annual Meeting of the American Society of Hematology in San Diego.  “Patients with NTDT” could include some individuals with beta thalassemia intermedia, […]

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"Nutrition and Thalassemia" Webinar Available Online

February 10, 2011 – Dr. Ellen B. Fung’s informative and valuable presentation on “Nutrition and Thalassemia,” the subject of CAF’s first webinar, is now available for viewing on the CAF website.   Dr. Fung (PhD, RD, CCD), who is am Associate Clinical Research Scientist  at Children’s Hospital & Research Center, Oakland and an Associate Adjunct […]

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