UCSF Needs Patient Feedback for Survey on In Utero Stem Cell Transplantation
July 16, 2020 – The University of California San Francisco (UCSF) has been conducting a clinical trial of in utero hematopoietic stem cell transplantation for fetuses that have been diagnosed with Alpha Thalassemia Major. They are now considering the possibility of expanding this trial to also include fetuses which have been diagnosed with Beta Thalassemia Major.
The team at UCSF would therefore appreciate the input of patients, and parents of patients, living with Beta Thalassemia Major regarding their attitudes towards in utero therapy for Beta Thalassemia Major. This input will be extremely helpful to UCSF as they consider designing a clinical trial protocol to offer transplants to fetuses who have been diagnosed with Beta Thalassemia Major. The survey takes approximately 6 minutes to complete, and can be found at: https://ucsf.co1.qualtrics.com/jfe/form/SV_8q1ZWvagXhrqrwV